Treatment introduces an expansion of the scope of gene therapies that might lead to similar treatments for neurodegenerative ...

I cried with every single patient,” Sung says. “It just was this crazy feeling that, for the patients and families, almost can’t feel real.” The treatment, known as AMT-130, is delivered deep into the ...

How cell and gene therapy developers can lessen the chances of receiving FDA complete response letters through the use of proactive chemistry, manufacturing, and controls strategies.

In a preclinical study, UC Davis Comprehensive Cancer Center scientists have developed a highly targeted gene therapy that ...

After years of heartbreak, researchers have found an experimental treatment that can slow the progression of Huntington’s ...

A gene-editing therapy led to durable changes in serum transthyretin levels among people with hereditary transthyretin ...

Stunning success in halting Huntington's disease with gene therapy offers new hope to those with the disorder—and potential ...

From cancer biology to proactive health management, customized care is changing patient outcomes, but what are the costs and ...

A one-time gene therapy called AMT-130 helped slow the progression of Huntington's disease by 75%, paving the way for the ...

Becoming a millionaire through stock investing is possible, but it requires patience, discipline, and the acumen to make informed investment choices. Not every company can generate the kind of returns ...