Stanford researchers and their collaborators have revealed a new device that could change the way scientists conduct ...

Stunning success in halting Huntington's disease with gene therapy offers new hope to those with the disorder—and potential ...

A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the ...

"On the basis of these results, it seems likely AMT-130 will be the first licensed treatment to slow Huntington's disease, ...

How cell and gene therapy developers can lessen the chances of receiving FDA complete response letters through the use of ...

MasterControl research shows 40% of advanced therapy executives aren't confident they can meet CGT demand over the next three ...

Scientists have reversed diabetic heart failure with a genetic therapy in mice and a miniature human hearts made from stem ...

VectorBuilder, a global leader in the gene delivery space, has won two prestigious awards at the Asia-Pacific Cell and Gene ...

It's a test of CEO Bill Anderson's development credentials as patent expiries on blockbuster drugs threaten the group's ...

AMT-130 gene therapy slowed Huntington’s progression by 75%, offering the first evidence of a disease-modifying treatment.

After years of heartbreak, researchers have found an experimental treatment that can slow the progression of Huntington’s ...

The lab-generated eggs could be fertilized with sperm, but were riddled with chromosomal abnormalities. Most embryos stopped ...