Stunning success in halting Huntington's disease with gene therapy offers new hope to those with the disorder—and potential ...

From cancer biology to proactive health management, customized care is changing patient outcomes, but what are the costs and ...

Life sciences ranked among the top four sectors, with a notable rise of companies integrating AI and biotech in ...

The new therapy is being hailed as a breakthrough. But the small study has some limitations – and hasn’t been peer-reviewed.

A company called uniQure has announced promising results from a trial of a new gene therapy for Huntington's disease. The ...

As well as slowing disease progression by 75 percent at 36 months, the scientists found that neurofilament light protein (NfL)—a biomarker of neuronal damage—levels in spinal fluid were lower in ...

Stanford researchers and their collaborators have revealed a new device that could change the way scientists conduct ...

The first participant in an investigational gene therapy trial of STXBP1 encephalopathy died, Capsida Biotherapeutics said. The death occurred days after dosing, according to information posted on the ...

September is Sickle Cell Awareness Month, and millions of people worldwide are living with the disease. But advances in ...

Scientists reported positive results on a trial for a potential Huntington's disease treatment Sept. 24, 2025. Here's what to know.

Read here for analysis of the growth potential of MeiraGTx (MGTX) stock's gene therapy pipeline and Hologen partnership for ...

Doctors in UK say gene therapy for Huntington’s disease slowed its progress 75%; may help other neurocognitive ills ...