Thanks to in-utero blood transfusion technology, what was once a fatal diagnosis in the womb can now result in live births. However, this medical advancement created a new challenge: a growing ...
GeneDx CEO Katherine Stueland explains how her company screens babies’ DNA for mutations that cause thousands of treatable ...
Ten-year-old Sebastian Veiman is racing against time to receive €2.5 million gene therapy that could halt — or even reverse — ...
Preliminary results from a small trial offer the clearest evidence yet that the brain disease’s progression can be slowed.
An experimental gene therapy was found to slow the progression of Huntington’s disease in a “pivotal” study, according to drugmaker uniQure, marking a major step toward a potential first genetic ...
This article is part of Nature Outlook: Skin, an editorially independent supplement produced with financial support from LEO Pharma. About this content. KaDee Troop is the mother of seven adopted ...
Health on MSN
What To Know About Hemophilia, a Rare Blood Disorder
Hemophilia is a rare medical condition where blood doesn't clot properly because the body lacks certain clotting factors.
WCMH Columbus on MSN
Columbus family continues to raise awareness for daughter’s rare disorder
Since we last saw Lo, she has hit a lot of milestones. Lo, 5, just started kindergarten and her parents said her ...
A recent milestone study used the LNP delivery system developed by Acuitas Therapeutics to treat a newborn with urea cycle ...
Winsights.life envisions a HIPAA-protected space where families own their health data, track their child's progress, and ...
The seventh annual Calves to Cure DMD charity cattle auction raised funds to help fund research for Duchenne muscular ...
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