I cried with every single patient,” Sung says. “It just was this crazy feeling that, for the patients and families, almost can’t feel real.” The treatment, known as AMT-130, is delivered deep into the ...

How cell and gene therapy developers can lessen the chances of receiving FDA complete response letters through the use of proactive chemistry, manufacturing, and controls strategies.

After years of heartbreak, researchers have found an experimental treatment that can slow the progression of Huntington’s ...

Stunning success in halting Huntington's disease with gene therapy offers new hope to those with the disorder—and potential ...

From cancer biology to proactive health management, customized care is changing patient outcomes, but what are the costs and ...

Becoming a millionaire through stock investing is possible, but it requires patience, discipline, and the acumen to make informed investment choices. Not every company can generate the kind of returns ...

An update from Genflow Biosciences Plc ( ($GB:GENF) ) is now available. Genflow Biosciences Plc reported significant advancements in its human and ...

Companies are moving from using AI for distinct operations to applying the technology for control and optimization of the ...

Stunning success in halting Huntington's disease with gene therapy offers new hope to those with the disorder—and promises ...

This eBook will go beyond just talking about how to streamline manufacturing but also provide in-depth insights into topics that aren’t always covered to the same degree but are just as important to ...

As well as slowing disease progression by 75 percent at 36 months, the scientists found that neurofilament light protein (NfL)—a biomarker of neuronal damage—levels in spinal fluid were lower in ...