Stanford researchers and their collaborators have revealed a new device that could change the way scientists conduct ...

A gene therapy trial claims to show promising results for patients with Huntington’s disease. A press announcement of the experimental treatment suggests significant slowing of the disease over three ...

From cancer biology to proactive health management, customized care is changing patient outcomes, but what are the costs and ...

A company called uniQure has announced promising results from a trial of a new gene therapy for Huntington's disease. The ...

Scientists from Tel Aviv University and Boston Children's Hospital use a optimized virus to deliver a corrected gene into the ...

Doctors in UK say gene therapy for Huntington’s disease slowed its progress 75%; may help other neurocognitive ills ...

The new therapy is being hailed as a breakthrough. But the small study has some limitations – and hasn’t been peer-reviewed.

As well as slowing disease progression by 75 percent at 36 months, the scientists found that neurofilament light protein (NfL)—a biomarker of neuronal damage—levels in spinal fluid were lower in ...

September is Sickle Cell Awareness Month, and millions of people worldwide are living with the disease. But advances in ...

Scientists have developed functional eggs from ordinary human skin cells, a proof of concept that could open up new ways to ...

Ten-year-old Sebastian Veiman is racing against time to receive €2.5 million gene therapy that could halt — or even reverse — ...

Read here for analysis of the growth potential of MeiraGTx (MGTX) stock's gene therapy pipeline and Hologen partnership for ...