Stanford researchers and their collaborators have revealed a new device that could change the way scientists conduct ...

Being proactive — especially when it comes to testing, process development and preparing for commercialization — can greatly decrease the risk that your CGT will receive a CRL.

How cell and gene therapy developers can lessen the chances of receiving FDA complete response letters through the use of ...

Gene therapy is a revolutionary field in modern medicine, offering transformative potential to treat and potentially cure a wide range of genetic and acquired diseases. By addressing the root cause of ...

A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the ...

At the European Cell & Gene Therapy Summit 2025, funding challenges and innovation drove discussions on the sector’s future.

Results from a three-year trial suggest an experimental gene therapy for Huntington's disease can slow the progression of the deadly condition by 75%.

The gene therapy company uniQure has announced top-level data from its trial of AMT-130, a new gene therapy designed to treat ...

Jesse Gelsinger died after receiving a gene therapy treatment to treat a liver disease. The death sparked an investigation ...

Scientists have reversed diabetic heart failure with a genetic therapy in mice and a miniature human hearts made from stem ...

In a trial of people with early Huntington's, the newly developed therapy slowed the progression of symptoms by 75%.

VectorBuilder, a global leader in the gene delivery space, has won two prestigious awards at the Asia-Pacific Cell and Gene ...