A gene therapy trial claims to show promising results for patients with Huntington’s disease. A press announcement of the experimental treatment suggests significant slowing of the disease over three ...

A company called uniQure has announced promising results from a trial of a new gene therapy for Huntington's disease. The ...

September is Sickle Cell Awareness Month, and millions of people worldwide are living with the disease. But advances in ...

As well as slowing disease progression by 75 percent at 36 months, the scientists found that neurofilament light protein (NfL)—a biomarker of neuronal damage—levels in spinal fluid were lower in ...

Doctors in the United Kingdom say they have found a gene therapy treatment to slow the progression of the devastating illness ...

Scientists reported positive results on a trial for a potential Huntington's disease treatment Sept. 24, 2025. Here's what to know.

Stanford researchers and their collaborators have revealed a new device that could change the way scientists conduct ...

At the European Cell & Gene Therapy Summit 2025, funding challenges and innovation drove discussions on the sector’s future.

Researchers from the Department of Biomedical Engineering at UNIST and the Center for Genomic Integrity at the Institute for Basic Science (IBS) have announced an advance in cancer gene therapy. Their ...

Scientists from Tel Aviv University and Boston Children's Hospital use a optimized virus to deliver a corrected gene into the ...

UC Davis Health researchers are testing a new gene therapy that could be transformational for patients with Angelman syndrome ...