A company called uniQure has announced promising results from a trial of a new gene therapy for Huntington's disease. The ...
In 2014, musician Eddie Vedder and Jill McCormick Vedder co-founded the EB Research Partnership,a non-profit organization ...
Preliminary results from a small trial offer the clearest evidence yet that the brain disease’s progression can be slowed.
An experimental gene therapy slowed the progression of Huntington’s disease by 75% after three years — study results likely ...
“This result changes everything,” said principal investigator Professor Ed Wild, from UCL’s Huntington’s Disease Centre. “On ...
This week on "The Readout LOUD" podcast: a gene therapy success in Huntington's, Trump's autism announcement, and more.
A one-time experimental treatment shows unprecedented success in slowing Huntington's disease, according to UCL researchers.
Until recently, even the most advanced gene therapies could only be given after a child was born—often racing against time to prevent irreversible damage. In the first part of this series, we explored ...
A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the ...
The search for gene therapies to treat rheumatoid arthritis (RA) has moved in fits and starts over the past two decades, with trials starting and stopping, and their focus shifting to osteoarthritis ...